Therapeutic Areas

Rare Diseases

Alport syndrome
C3G dense deposit disease and C3 glomerulonephritis
Duchenne muscular dystrophy
Familial hypercholesterolemia
Gaucher disease
hATTR amyloidosis
Hemophilia A and B
Hepatic porphyrias
Myasthenia Gravis
Paroxysmal Nocturnal Hemoglobinuria
Pyruvate kinase deficiency
Tuberous sclerosis
WHIM syndrome

Hematology / Oncology

Bladder cancer
Chronic lymphocytic leukemia (CLL)
Chronic myelogenous leukemia (CML)
Cancer metabolism
CAR-T therapy
Follicular lymphoma (FL)
Gastrointestinal
Mantle cell lymphoma (MCL)
Melanoma
Metastatic castration-resistant prostate cancer
Non-small cell lung cancer
Renal cell carcinoma
Secondary immunodeficiency (SID) from immunotherapy
Y-90 resin microspheres for the treatment of liver metastases

Additional subject areas

Allergy and chronic inflammation
Antibiotic Resistance and Stewardship
Asthma
Attention deficit hyperactivity disorder
Autoimmune diseases
Cardiovascular disease
Chronic idiopathic urticaria
Chronic kidney disease
Chronic liver disease
Common variable immunodeficiency
Complement-mediated diseases
Cystic fibrosis
Dermatology
Diabetes
Gene therapy
Hypothyroidism
Inclusion-body myositis
Liquid biopsy
Multiple sclerosis
Neurological disorders
Ophthalmology
Osteoarthritis
Polycythemia vera
Primary immune deficiency
Pyruvate kinase deficiency (PKD)
Transplant Medicine
Traumatic brain injury

Aesthetic Medicine

Fillers
Absorbable suspension sutures
Microfocused ultrasound
Radiofrequency for tissue tightening